Apply to trial NCT06891443

A few quick questions so the study team can decide if you might be a fit.

RecruitingPhase 3Drug trial

Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)

The purpose of this double-masked, randomized, placebo-controlled, paired-eye study is to evaluate the efficacy, safety and tolerability of Sepofarsen in subjects with Leber Congenital Amaurosis (LCA) due to the c.2991+1655A\>G (p.Cys998X) mutation in the CEP290.

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Answer a few questions
About 5 to 10 minutes. Skip-friendly where possible.
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When a site picks up your application, we introduce you to their team directly — with you on the thread.
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Study to Evaluate Sepofarsen in Subjects With Leber Congenital Amaurosis (LCA) Type 10 (HYPERION)

How this works

Answer a few questions

We connect you with the study team

The team reaches out to schedule screening