A Long-term Extension Study to Assess the Long-term Safety and Efficacy of Pegtibatinase Treatment in Participants ≥5 to ≤65 Years of Age With Classical Homocystinuria (HCU) (ENSEMBLE)
for Homocystinuria
13 locations incl. Phoenix
Sponsor: Travere Therapeutics, Inc.
Sex: All·Age: 5 - 65
Code: NCT06431893·Phase 3·Enrolling By Invitation