Duchenne Muscular Dystrophy — Trials, FDA Actions & Pivotal Research

20 active Duchenne Muscular Dystrophy trials currently recruiting in the US, sourced from ClinicalTrials.gov.

Synced daily from openFDA and ClinicalTrials.gov. Last sync: August 19, 2026.

Find recruiting Duchenne muscular dystrophy trials near you

Recruiting trials by city

Cities where Duchenne Muscular Dystrophy trials in our archive had recruiting sites. Each link lists every currently recruiting paid clinical trial at that location.

Little Rock, AR Gainesville, FL Boston, MA Aurora, CO Chicago, IL Los Angeles, CA

Active Duchenne Muscular Dystrophy trials

Currently recruiting US trials matching Duchenne Muscular Dystrophy, sourced live from ClinicalTrials.gov. We’ll add per-event articles here as those trials post results or hit primary completion.

Safety and Efficacy of KER-065 in Participants With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Keros Therapeutics, Inc.

Sex: Male·Age: 9+

Code: NCT07704099·Phase 2·Not Yet Recruiting·Listed Jul 15, 2026

A Phase 3 Study to Evaluate the Safety and Efficacy of AOC 1044 (Also Referred to as Delpacibart Zotadirsen) in Participants With DMD With Gene Mutations Amenable to Exon 44 Skipping

for Muscular Dystrophies

Sponsor: Avidity Biosciences, Inc.

Sex: Male·Age: 7 - 16

Code: NCT07587242·Phase 3·Recruiting·Listed May 2026

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Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne Muscular Dystrophy Treated in a Post-Marketing Setting

for Duchenne Muscular Dystrophy

Sponsor: Sarepta Therapeutics, Inc.

Sex: Male·Age: 4+

Code: NCT07542314·Phase 4·Not Yet Recruiting·Listed Apr 2026

Evaluating VM100 Nutritional Supplement for Improving Quality of Life in Duchenne Muscular Dystrophy Patients

for Duchenne Muscular Dystrophy

1 location in Gainesville

Sponsor: University of Florida

Sex: Male·Age: 6+

Code: NCT07766980·Recruiting·Listed Aug 17, 2026

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Efficacy, Safety, and Tolerability of Zeleciment Rostudirsen (DYNE-251) Administered Intravenously Every 4 Weeks in Ambulatory Participants With Duchenne Muscular Dystrophy (FORZETTO)

for Duchenne Muscular Dystrophy (DMD)

1 location in Hillsborough

Sponsor: Dyne Therapeutics

Sex: Male·Age: 4 - 18

Code: NCT07608432·Phase 3·Recruiting·Listed May 2026

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Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Wave Life Sciences USA, Inc.

Sex: Male·Age: All ages

Code: NCT07209332·Phase 2·Enrolling By Invitation·Listed Oct 2025

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

for Duchenne Muscular Dystrophy

7 locations incl. Los Angeles

Sponsor: Satellos Bioscience, Inc.

Sex: Male·Age: 7 - 9

Code: NCT07287189·Phase 2·Recruiting·Listed Dec 2025

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A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

for Duchenne Muscular Dystrophy

3 locations incl. Little Rock

Sponsor: Solid Biosciences Inc.

Sex: Male·Age: 7 - 11

Code: NCT07160634·Phase 3·Recruiting·Listed Sep 2025

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A Study to Evaluate the Tolerability, Safety and Efficacy of GNR-097 Gene Therapy in Pediatric Patients With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: AO GENERIUM

Sex: Male·Age: 4 - 9

Code: NCT07673809·Phase 1, Phase 2·Recruiting·Listed Jun 29, 2026

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A Clinical Study to Evaluate the Safety, Tolerability, and Efficacy of BBM-D101 in the Treatment of Duchenne Muscular Dystrophy.

for DMD

Sponsor: Belief BioMed (Beijing) Co., Ltd

Sex: Male·Age: 4 - 9

Code: NCT07058662·Phase 1, Phase 2·Recruiting·Listed Jul 2025

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A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

for Duchenne Muscular Dystrophy

10 locations incl. Little Rock

Sponsor: Insmed Gene Therapy LLC

Sex: Male·Age: 2 - 4

Code: NCT06817382·Phase 1·Recruiting·Listed Feb 2025

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Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Başak Çağla Arslan

Sex: Male·Age: 13 - 18

Code: NCT06402942·Recruiting·Listed May 2024

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Trial of Cell Based Therapy for DMD

for Duchenne Muscular Dystrophy

1 location in Minneapolis

Sponsor: Masonic Cancer Center, University of Minnesota

Sex: All·Age: 18+

Code: NCT06692426·Phase 1·Recruiting·Listed Nov 2024

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Investigation of the Relationship Between Executive Functions and Occupational Performance of Children With Duchenne Muscular Dystrophy

for Executive Dysfunction

Sponsor: Lokman Hekim University

Sex: Male·Age: 6 - 12·Accepts healthy volunteers

Code: NCT06868784·Enrolling By Invitation·Listed Mar 2025

Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.

for Duchenne Muscular Dystrophy

Sponsor: University of Malaga

Sex: All·Age: 5 - 20

Code: NCT06363526·Enrolling By Invitation·Listed Apr 2024

Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old

for Duchenne Muscular Dystrophy

Sponsor: Italfarmaco

Sex: Male·Age: 2 - 6

Code: NCT06769633·Phase 2·Recruiting·Listed Jan 2025

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Evaluation of Brain Dysfunction in Patients with Duchene Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Assiut University

Sex: Male·Age: 5 - 18·Accepts healthy volunteers

Code: NCT06732011·Not Yet Recruiting·Listed Dec 2024

The U.K. NorthStar Clinical Network

for Duchenne Muscular Dystrophy

Sponsor: University College, London

Sex: Male·Age: Up to 99

Code: NCT06711692·Not Yet Recruiting·Listed Dec 2024

Development of a Registry to Assess Natural History in Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Sex: Male·Age: All ages

Code: NCT06579859·Not Yet Recruiting·Listed Aug 2024

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

for Duchenne Muscular Dystrophy

31 locations incl. Phoenix

Sponsor: Catalyst Pharmaceuticals, Inc.

Sex: Male·Age: 2+

Code: NCT06564974·Recruiting·Listed Aug 2024

Apply to this trial