Selumetinib Paediatric NF1 Japan Study
- Sponsor
- AstraZeneca
- Study ID
- NCT04495127
- Phase
- PHASE1
- Status
- Completed
Conditions
- Neurofibromatosis Type 1
Eligibility Criteria
- Sex
- ALL
- Age
- 3 Years - 18 Years
- Healthy Volunteers
- Not accepted
Interventions
- Selumetinib — DRUGSelumetinib 25 mg/m2 BID
Study Details
This is a phase I open label study designed to evaluate the safety, tolerability, PK and efficacy of selumetinib in Japanese paediatric patients with neurofibromatosis type 1 and inoperable and symptomatic plexiform neurofibroma.
Key Dates
- Start date
- Aug 31, 2020
- Status verified
- Apr 2023
- Primary completion
- Jun 16, 2021
- Completion
- Mar 24, 2023
Study Design
- Enrollment
- 12 participants (actual)
- Allocation
- NA
- Intervention model
- SINGLE_GROUP
- Primary purpose
- TREATMENT
Arms
- Experimental: Selumetinib
Primary Outcome Measure
Safety and tolerability in terms of adverse events [ Time Frame: From obtaining the first informed consent until 30 days after the last dose (Selumetinib). Expected duration is approximately 2 years. ]
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