To Evaluate Efficacy and Safety of Parsaclisib and Ruxolitinib in Participants With Myelofibrosis Who Have Suboptimal Response to Ruxolitinib (LIMBER-304)

Part of paid clinical trials in Berkeley, California.

Sponsor
Incyte Corporation
Study ID
NCT04551053
Phase
PHASE3
Status
Terminated

Conditions

  • Myelofibrosis
  • Post Essential Thrombocythemia Myelofibrosis
  • Post Polycythemia Vera Myelofibrosis
  • Primary Myelofibrosis

Eligibility Criteria

Sex
ALL
Age
18 Years - N/A
Healthy Volunteers
Not accepted

Interventions

  • parsaclisib — DRUG
    parsaclisib will be administered QD orally
  • ruxolitinib — DRUG
    ruxolitinib will be administered BID orally
  • placebo — DRUG
    placebo will be administered QD orally

Study Details

The purpose of the study is to compare the efficacy and safety of parsaclisib when combined with ruxolitinb versus placebo combined with ruxolitinib in participants with myelofibrosis who have suboptimal response while receiving ruxolitinib monotherapy.

Key Dates

Start date
May 26, 2021
Status verified
Sep 2025
Primary completion
Aug 16, 2023
Completion
Aug 21, 2024

Study Design

Enrollment
177 participants (actual)
Allocation
RANDOMIZED
Intervention model
PARALLEL
Primary purpose
TREATMENT

Arms

  • Experimental: Group A : ruxolitinib +parsaclisib
    Participants will receive parsaclisib starting from Day 1 for the duration of study, while continuing to receive the stable dose of ruxolitinib they were taking for the 8 weeks prior to Day 1.
  • Placebo Comparator: Group B : ruxolitinib + placebo
    Participants will receive placebo starting from Day 1 for the duration of study, while continuing to receive the stable dose of ruxolitinib they were taking for the 8 weeks prior to Day 1.

Primary Outcome Measure

Percentage of Participants Achieving ≥25% Reduction in Spleen Volume From Baseline to Week 24 as Measured by Magnetic Resonance Imaging (MRI) (or Computed Tomography [CT] Scan in Applicable Participants) [ Time Frame: Baseline; Week 24 ]

Locations (35)

FacilityCityStateZIPSite coordinators
Sutter Health Alta Bates Summit Medical Center Absmc Alta Bates Summit Comprehensive Cancer CenterBerkeleyCalifornia94704-
CCAREFresnoCalifornia93720-
California Research Institute (Cri)Los AngelesCalifornia90027-6005-
Emad Ibrahim Md IncRedlandsCalifornia92373-
Scripps ClinicSan DiegoCalifornia92103-
Coastal Integrated Cancer Care - CiccSan Luis ObispoCalifornia93401-
Stamford Hospital - Medical Oncology HematologyStamfordConnecticut06904-
Georgetown UniversityWashington D.C.District of Columbia20057-
Emory UniversityAtlantaGeorgia30322-
Augusta University - Medical College of GeorgiaAugustaGeorgia30912-
Indiana University Melvin and Bren Simon Cancer CenterIndianapolisIndiana46202-
University of Kansas Hospital AuthorityWestwoodKansas66205-
Tulane UniversityNew OrleansLouisiana70112-
Beth Israel Deaconess Medical CenterBostonMassachusetts02215-
Massachusetts General HospitalBostonMassachusetts02114-
Midamerica Cancer CareKansas CityMissouri64114-
New Jersey Hematology Oncology Associates LlcBrickNew Jersey08724-
Morristown Medical Center - Atlantic Health SystemMorristownNew Jersey07960-
Westchester Medical Center Advanced OncologyHawthorneNew York10532-
Memorial Sloan Kettering Cancer CenterNew YorkNew York10065-
Mount Sinai School of MedicineNew YorkNew York10029-
Montefiore Medical CenterThe BronxNew York10467-
Advent Health Hendersonville Park Ridge Hospital HendersonvilleClydeNorth Carolina28721-
Duke Cancer CenterDurhamNorth Carolina27710-
Cleveland ClinicClevelandOhio44195-
Oregon Health & Science UniversityColumbusOhio43210-
Oregon Health & Science UniversityPortlandOregon97239-
Hillman Cancer CenterPittsburghPennsylvania15232-
Baptist Cancer CenterMemphisTennessee38120-
Texas Oncology - Baylor Sammons Cancer CenterDallasTexas75246-2092-
Texas Oncology - Medical City DallasDallasTexas75230-
University of Texas Southwestern Medical CenterDallasTexas75390-8565-
Kelsey Seybold ClinicHoustonTexas77025-
Renovatio ClinicalHoustonTexas77005-
Providence Regional Medical Center EverettEverettWashington98201-

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