A Study to Provide Continued Access to Mitapivat for Participants Who Previously Completed an Agios-Sponsored Mitapivat Study
- Sponsor
- Agios Pharmaceuticals, Inc.
- Study ID
- NCT05777993
- Phase
- PHASE4
- Status
- Enrolling By Invitation
Conditions
- Anemia, Hemolytic
- Pyruvate Kinase Deficiency
Eligibility Criteria
- Sex
- ALL
- Age
- 18 Years - N/A
- Healthy Volunteers
- Not accepted
Interventions
- Mitapivat — DRUGTablets
Study Details
The purpose of this study is to provide continued access to mitapivat for participants who completed an Agios-sponsored mitapivat study (antecedent) and do not have commercial access to mitapivat.
Key Dates
- Start date
- Jul 6, 2023
- Status verified
- Mar 2026
- Primary completion
- Aug 31, 2029
- Completion
- Aug 31, 2029
Study Design
- Enrollment
- 6 participants (estimated)
- Allocation
- NA
- Intervention model
- SINGLE_GROUP
- Primary purpose
- TREATMENT
Arms
- Experimental: MitapivatParticipants will receive mitapivat of 5, 20 or 50 milligrams (mg), orally, twice daily (BID), based on the last dose received by the participants in the antecedent study. Mitapivat will be administered from Day 1 up to end of treatment period of this study.
Primary Outcome Measure
Percentage of Participants With Adverse Events (AEs) and Serious Adverse Events (SAEs) [ Time Frame: Up to approximately 6.2 years ]
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