A Study Evaluating the Effectiveness and Safety of Risdiplam Administered as an Early Intervention in Pediatric Participants With Spinal Muscular Atrophy After Gene Therapy
for Muscular Atrophy, Spinal
Sites in Fort Worth, Dallas +8 more locations
Sponsor: Hoffmann-La Roche
Sex: All·Age: 3 Months - 24 Months
Code: NCT05861986·Phase 4·Recruiting·Listed May 2023