A Study Evaluating the Effectiveness and Safety of Risdiplam Administered in Pediatric Patients With Spinal Muscular Atrophy Who Experienced a Plateau or Decline in Function After Gene Therapy
for Muscular Atrophy, Spinal
Sites in Grand Rapids +8 more locations
Sponsor: Hoffmann-La Roche
Sex: All·Age: 3 Months - 24 Months
Code: NCT05861999·Phase 4·Recruiting·Listed May 2023