A Study to Evaluate How Apitegromab Works in Subjects Who Are Less Than 2 Years Old and Have Spinal Muscular Atrophy
for Spinal Muscular Atrophy
Drug: Apitegromab
Sites in Memphis +13 more locations
Sponsor: Scholar Rock, Inc.
Sex: All·Age: Up to 2
Code: NCT07047144·Phase 2·Recruiting·Listed Jul 2025