A Long-term Study for the Outcome of Pompe Disease

Sponsor
National Taiwan University Hospital
Study ID
NCT02399748
Status
Recruiting
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Conditions

Eligibility Criteria

Sex
ALL
Age
N/A - N/A
Healthy Volunteers
Not accepted

Study Details

Prospectively follow patients with Pompe disease underwent enzyme replacement therapy.

Key Dates

Start date
Apr 30, 2007
Status verified
Jul 2017
Primary completion
Dec 31, 2026
Completion
Dec 31, 2026

Study Design

Enrollment
50 participants (estimated)

Primary Outcome Measure

all cause morbidities [ Time Frame: 10 years ]

Central Contacts

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