Disease Progression in Women With X-linked Adrenoleukodystrophy

Sponsor
Minoryx Therapeutics, S.L.
Study ID
NCT06178120
Status
Recruiting

Conditions

Eligibility Criteria

Sex
FEMALE
Age
18 Years - N/A
Healthy Volunteers
Not accepted

Study Details

Observational, single-site prospective and minimally interventional study in women with X-linked adrenoleukodystrophy (ALD), conducted in France.

Key Dates

Start date
Jan 2, 2024
Status verified
Dec 2023
Primary completion
Dec 31, 2026
Completion
Jun 30, 2027

Study Design

Enrollment
40 participants (estimated)

Primary Outcome Measure

Spinal cord magnetization transfer ratio (MTR) [ Time Frame: Change from baseline up to 2 years ]

Central Contacts

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