An Open-label Extension Study to Evaluate Subcutaneous Zilucoplan in Pediatric Participants With Generalized Myasthenia Gravis
- Sponsor
- UCB Biopharma SRL
- Study ID
- NCT06435312
- Phase
- PHASE3
- Status
- Enrolling By Invitation
Conditions
- Generalized Myasthenia Gravis
Eligibility Criteria
- Sex
- ALL
- Age
- 12 Years - N/A
- Healthy Volunteers
- Not accepted
Interventions
- Zilucoplan — DRUGZilucoplan will be administered subcutaneously to pediatric study participants
Study Details
The purpose of this study is to assess the long-term safety and tolerability of an additional 52 weeks of Zilucoplan treatment administered by subcutaneous injection once daily in pediatric study participants
Key Dates
- First listed
- May 30, 2024
- Start date
- Nov 19, 2024
- Status verified
- Jul 2026
- Primary completion
- Oct 26, 2027
- Completion
- Nov 19, 2027
Study Design
- Enrollment
- 8 participants (estimated)
- Allocation
- NA
- Intervention model
- SINGLE_GROUP
- Primary purpose
- TREATMENT
Arms
- Experimental: Zilucoplan ArmStudy participants will receive Zilucoplan at a pre-defined dose based on their weight.
Primary Outcome Measure
Occurence of treatment emergent adverse events during the course of the study [ Time Frame: Baseline (Day 1) to Safety Follow-up (up to Week 60) ]
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