Expansion Study of ALT001 in Patients With Multiple System Atrophy
- Sponsor
- yilong Wang
- Study ID
- NCT07476352
- Phase
- EARLY_PHASE1
- Status
- Not Yet Recruiting
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Conditions
- Multiple System Atrophy
Eligibility Criteria
- Sex
- ALL
- Age
- 30 Years - 75 Years
- Healthy Volunteers
- Not accepted
Interventions
- ALT001 — DRUG"ALT001" is a nerve repair protein developed by Darwin Start (Hubei) Biopharmaceutical Co., Ltd. It is a group of specific microenvironmental protein polymers secreted under the emergency conditions of stem cells. It has the advantages of selective assembly, targeted delivery, efficient repair of damaged tissues, high safety, chemical stability, easy storage, etc., and has a powerful neural repair function. According to the groups, patients would be treated with ALT001 via intrathecal injection or intravenous injection. Intravenous administration of ALT001 was given to each MSA patient in the intervention group, with intravenous administration on days 1 to 14, 31 to 44±3 and 61 to 74±5, and treatment was given once a day. Intravenous administration: ALT001 (130 μg/branch) was dissolved in 100 ml sodium chloride injection, which was completed in about 30-40 minutes.
Study Details
This is an open-label, single-center, prospective, single-arm clinical study. The primary objective of this study is to evaluate the safety, tolerability, and preliminary efficacy of ALT001 in the treatment of patients with multiple system atrophy (MSA) in a real-world setting.
Key Dates
- First listed
- Mar 17, 2026
- Start date
- May 6, 2026
- Status verified
- Mar 2026
- Primary completion
- Oct 30, 2027
- Completion
- Oct 30, 2027
Study Design
- Enrollment
- 60 participants (estimated)
- Allocation
- NA
- Intervention model
- SINGLE_GROUP
- Primary purpose
- TREATMENT
Arms
- Experimental: Intervention groupIntravenous administration of ALT001 was given to each MSA patient in the intervention group, with intravenous administration on days 1 to 14, 31 to 44±3 and 61 to 74±5, and treatment was given once a day. Intravenous administration: ALT001 (130 μg/branch) was dissolved in 100 ml sodium chloride injection, which was completed in about 30-40 minutes.
Primary Outcome Measure
The incidence of adverse events (AEs) and serious adverse events (SAEs) [ Time Frame: Day 180±7 after treatment ]
Central Contacts
- Weiqi Chen8615652813380
- Yahui Zhu8613439182912
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