BAG3-DCM Natural History Study
- Sponsor
- Rocket Pharmaceuticals Inc.
- Study ID
- NCT07486752
- Status
- Not Yet Recruiting
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Conditions
- Cardiovascular Diseases
- Dilated Cardiomyopathy (DCM)
- Genetic Diseases
- Heart Diseases
Eligibility Criteria
- Sex
- ALL
- Age
- 18 Years - N/A
- Healthy Volunteers
- Not accepted
Study Details
The goal of this international observational study is to learn about the natural history of Dilated Cardiomyopathy (DCM) arising from pathogenic BAG3 variants in adult patients ≥18 years of age.
Key Dates
- First listed
- Mar 20, 2026
- Start date
- May 31, 2026
- Status verified
- Mar 2026
- Primary completion
- Dec 31, 2032
- Completion
- Mar 31, 2033
Study Design
- Enrollment
- 30 participants (estimated)
Arms
- Arm: Prospective Cohort and Retrospective (Non Interventional)
Primary Outcome Measure
Cardiac structure and function [ Time Frame: 48 months ]
Central Contacts
- Clinical Information646-627-0033
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