Efficacy and Safety of Butylphthalide in the Treatment of Multiple System Atrophy
- Sponsor
- Second Affiliated Hospital, School of Medicine, Zhejiang University
- Study ID
- NCT07518810
- Phase
- PHASE2/PHASE3
- Status
- Not Yet Recruiting
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Conditions
- Multiple System Atrophy
Eligibility Criteria
- Sex
- ALL
- Age
- 30 Years - 80 Years
- Healthy Volunteers
- Not accepted
Interventions
- 3-N-butylphthalide — DRUG3-n-Butylphthalide (NBP), also known as celery seed oil extract, is a lipid-soluble compound isolated from celery seeds. NBP was approved by the China Food and Drug Administration (CFDA) in 2002 for the treatment of acute ischemic stroke. NBP has demonstrated significant improvement in motor deficits and exhibited neuroprotective effects in animal models of various neurodegenerative diseases, such as Alzheimer's disease (AD), Parkinson's disease (PD), and amyotrophic lateral sclerosis (ALS). For NBP used in ENMSA trial, its dosage form is soft capsule, containing 100mg NBP per capsule. Application frequency will be three times a day, 2 capsules each time.
Study Details
The present study aims to conduct a randomized controlled trial to evaluate the efficacy and safety of 3-n-Butylphthalide (NBP) in improving symptoms in patients with Multiple System Atrophy (MSA). The main questions it aims to answer are: 1. To evaluate whether NBP soft capsules, compared with placebo, alleviates the major clinical symptoms in patients with MSA. 2. Whether NBP application is safe to treat patients with MSA. In this trial, NBP will be compared with placebo (similar soft capsule without effective component of NBP) to demonstrate if NBP can alleviates MSA symptoms Participants of ENMSA will: 1. Take NBP or Placebo three times a day for 6 months 2. Be served with clinical visit four times for follow-up and tests 3. Keep a diary of drug application and symptom changes
Key Dates
- First listed
- Apr 9, 2026
- Start date
- Apr 10, 2026
- Status verified
- Oct 2025
- Primary completion
- Apr 10, 2027
- Completion
- Oct 10, 2027
Study Design
- Enrollment
- 150 participants (estimated)
- Allocation
- RANDOMIZED
- Intervention model
- PARALLEL
- Primary purpose
- TREATMENT
Arms
- Experimental: NBP treatment groupParticipants in the NBP treatment group will receive NBP soft capsules (dosage form: 100 mg/capsule), two capsules per dose, three times daily (total daily dose of 600 mg). The whole treatment duration is six months, during which all patients will maintain their original medication unchanged.
- Placebo Comparator: Placebo control groupParticipants in the Placebo control group will receive two Placebo soft capsules each time, three times daily (total daily dose of 600 mg). The whole application duration is six months, during which all patients will maintain their original medication unchanged.
Primary Outcome Measure
Main symptom control of MSA [ Time Frame: Baseline; 1st, 3rd, 6th, 12th month after intervention initiation ]
Central Contacts
- Jiali Pu, MD+86 13989468062
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