RD06-05 Universal CD19/BCMA CAR-T for Refractory Pediatric Autoimmune Diseases
- Sponsor
- The Children's Hospital of Zhejiang University School of Medicine
- Study ID
- NCT07674147
- Phase
- EARLY_PHASE1
- Status
- Not Yet Recruiting
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Conditions
- Autoimmune Diseases
- IIM- Idiopathic Inflammatory Myopathies
- IgAN - IgA Nephropathy
- Multi-Drug Resistant Nephrotic Syndrome
- SLE - Systemic Lupus Erythematosus
- SSc-Systemic Sclerosis
Eligibility Criteria
- Sex
- ALL
- Age
- 5 Years - 20 Years
- Healthy Volunteers
- Not accepted
Interventions
- RD06-05 CART Cell Infusion — DRUGCAR T-cell therapy administered intravenously after a lymphodepleting therapy regimen consisting of fludarabine and cyclophosphamide.
Study Details
This is a single-arm, open-label, phase I clinical study to evaluate the safety, tolerability, pharmacokinetics, pharmacodynamics, and efficacy of RD06-05, a universal CD19/BCMA dual-targeting chimeric antigen receptor T-cell (CAR-T), in pediatric and adolescent patients with refractory autoimmune diseases, including systemic lupus erythematosus/lupus nephritis (SLE/LN), systemic sclerosis (SSc), idiopathic inflammatory myopathy (IIM), multidrug-resistant nephrotic syndrome (MDR-NS), and refractory IgA nephropathy (IgAN). Approximately 30 eligible patients will be enrolled and receive a single intravenous infusion of RD06-05 at an initial dose of 6×10⁶ CAR+ T cells/kg, with a potential dose escalation to 10×10⁶ CAR+ T cells/kg following review by a Safety Review Committee (SRC).
Key Dates
- First listed
- Jun 29, 2026
- Start date
- Jul 31, 2026
- Status verified
- Jun 2026
- Primary completion
- Jul 31, 2029
- Completion
- Jul 31, 2030
Study Design
- Enrollment
- 30 participants (estimated)
- Allocation
- NA
- Intervention model
- SINGLE_GROUP
- Primary purpose
- TREATMENT
Arms
- Experimental: RD06-05 Universal CAR-T TherapySingle-arm, open-label: participants receive a single intravenous infusion of RD06-05 (universal CD19/BCMA dual-targeting CAR-T cells) following a lymphodepleting regimen of fludarabine and cyclophosphamide.
Primary Outcome Measure
Incidence of Treatment-Emergent Adverse Events (TEAEs), Serious Adverse Events (SAEs), and Adverse Events of Special Interest (AESIs) [ Time Frame: From signing of informed consent through 90 days post-infusion (for related AEs, up to 24 months post-infusion) ]
Central Contacts
- Jianhua Mao+86 13516819071
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