Universal STAR-T Cell Injection in Generalized Myasthenia Gravis
- Sponsor
- Daishi Tian
- Study ID
- NCT07714798
- Phase
- PHASE1
- Status
- Not Yet Recruiting
Notify me when recruiting opens
Save your spot on the interest list for this study. We'll keep your details with this study so our team can follow up when recruiting opens.
Add your contact details and location so we can keep your interest tied to this study.
Conditions
- Generalized Myasthenia Gravis
Eligibility Criteria
- Sex
- ALL
- Age
- 18 Years - 65 Years
- Healthy Volunteers
- Not accepted
Interventions
- Universal STAR-T Cell — DRUGSubjects will receive infusion of Universal STAR-T Cells at the starting dose of 1.5E6 STAR+T cells/kg.
Study Details
This is a Phase I, single-arm, open-label, dose-escalation and dose-expansion study. This is an exploratory clinical study of universal STAR-T cell injection in patients with refractory generalized myasthenia gravis (GMG). Approximately 10-24 participants aged 18-65 years (inclusive) with the condition are planned to be enrolled. The primary objective is to evaluate the safety, tolerability, preliminary efficacy, pharmacokinetic/pharmacodynamic (PK/PD) profile, and immunogenicity of universal STAR-T cell injection. The starting dose is 1.5E6 STAR+ T cells/kg, administered as a single intravenous infusion.Based on safety, PK results, and preliminary efficacy data obtained from the initial dose cohorts, a recommended dose will be selected for subsequent dose-expansion studies to further systematically evaluate the safety and efficacy of universal STAR-T cell injection. This study includes the screening period (from D-28 to D-6), the pre-clearance treatment and rest observation period (from D-5 to D-1), the cell infusion and main study endpoint observation period (from D0 to W12 after infusion), and the follow-up period (from W12 after infusion to W104). The study is being conducted at Tongji Hospital, Tongji Medical College, Huazhong University of Science and Technology.
Key Dates
- First listed
- Jul 20, 2026
- Start date
- Jul 6, 2026
- Status verified
- Jul 2026
- Primary completion
- Jul 6, 2027
- Completion
- Jul 6, 2028
Study Design
- Enrollment
- 10 participants (estimated)
- Allocation
- NA
- Intervention model
- SINGLE_GROUP
- Primary purpose
- TREATMENT
Arms
- Experimental: Universal STAR-T CellSubjects will receive infusion of Universal STAR-T Cells at the starting dose of 1.5E6 STAR+T cells/kg.
Primary Outcome Measure
Type, severity, and frequency of Adverse Events (AEs) and Serious Adverse Events (SAEs). [ Time Frame: AEs observation will be follow-up for 24 weeks. The observation period is extended to 104 weeks. ]
Central Contacts
- Daishi Tian13607178809
Related Studies
- Registry of Participants With Generalized Myasthenia Gravis Treated With Alexion C5 Inhibition Therapies (C5ITs)Recruiting · Alexion Pharmaceuticals, Inc. · Birmingham, Alabama
- Evaluating the Pharmacokinetics, Pharmacodynamics, and Safety of Efgartigimod Administered Intravenously in Children With Generalized Myasthenia GravisPHASE2/PHASE3 · Recruiting · argenx · Chicago, Illinois
- Evaluating Long-term Safety of Efgartigimod Administered Intravenously and Efgartigimod PH20 Administered Subcutaneously in Children With Generalized Myasthenia GravisPHASE2/PHASE3 · Enrolling By Invitation · argenx · Chicago, Illinois
- A Study to Evaluate Subcutaneous Zilucoplan in Pediatric Participants With Generalized Myasthenia GravisPHASE2/PHASE3 · Recruiting · UCB Biopharma SRL · Chicago, Illinois