A Prospective Exploratory Study of the Safety and Preliminary Efficacy of the α-Syn H21 Monoclonal Antibody in Patients With Multiple System Atrophy
- Sponsor
- Ruijin Hospital
- Study ID
- NCT07774585
- Phase
- PHASE1
- Status
- Not Yet Recruiting
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Conditions
- Multiple System Atrophy
Eligibility Criteria
- Sex
- ALL
- Age
- 45 Years - 75 Years
- Healthy Volunteers
- Not accepted
Interventions
- α-Syn H21 Monoclonal Antibody — BIOLOGICALThe α-Syn H21 monoclonal antibody is a humanized monoclonal antibody designed to selectively bind pathological alpha-synuclein aggregates. Participants will receive the study drug by intravenous infusion once every 4 weeks for a total of 3 doses during the 12-week study period.
Study Details
Multiple system atrophy (MSA) is a progressive neurodegenerative disorder characterized by autonomic dysfunction, parkinsonism, and cerebellar ataxia. Abnormal aggregation of alpha-synuclein is believed to play an important role in disease progression. The α-Syn H21 monoclonal antibody is designed to selectively bind pathological alpha-synuclein aggregates and may reduce their spread and related neuroinflammation. This single-center, prospective, exploratory study will evaluate the safety, tolerability, and preliminary efficacy of the α-Syn H21 monoclonal antibody in patients with MSA. Participants will receive intravenous infusions of H21 every 4 weeks for 3 doses and will be followed for 12 weeks. Clinical symptoms, laboratory tests, imaging findings, and adverse events will be assessed to determine whether H21 may provide clinical benefit and support future larger studies.
Key Dates
- First listed
- Aug 19, 2026
- Start date
- Sep 15, 2026
- Status verified
- Apr 2026
- Primary completion
- Dec 31, 2026
- Completion
- Dec 31, 2026
Study Design
- Enrollment
- 3 participants (estimated)
- Allocation
- NA
- Intervention model
- SINGLE_GROUP
- Primary purpose
- TREATMENT
Arms
- Experimental: H21 Treatment
Primary Outcome Measure
Incidence of treatment-emergent adverse events [ Time Frame: From first dose through Week 12 ]
Central Contacts
- Jun Liu, MD, PhD021-86-64370045
- Yan SHEN, MD, PhD+86-021-64370045
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