Clinical Trials at UPMC Children's Hospital of Pittsburgh

As of June 2026, 52 paid clinical trials are recruiting at UPMC Children's Hospital of Pittsburgh in Pittsburgh, Pennsylvania. Compensation typically covers time, travel, and study visits — most studies also offer study-related medical care at no cost to participants.

Recruiting trial data synced daily from ClinicalTrials.gov. Last sync: June 3, 2026.

Filter results

Filter results

State

City

Facility

Phase

Study type

Intervention

Recruitment status

Condition

Sex

Age

Healthy volunteers only

52 clinical trials at UPMC Children's Hospital of Pittsburgh

·Clear filters·↓ Download CSV

Data Collection Study of Patients With Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT With RIC

for Primary Immunodeficiency (PID)

1 location in Pittsburgh

Sponsor: Paul Szabolcs

Sex: All·Age: 2 Months - 60

Code: NCT04528355·Recruiting

Apply to this trial

Genome Sequencing in the Intensive Care Unit Population

for Infant, Newborn, Disease

1 location in Pittsburgh

Sponsor: Jerry Vockley, MD, PhD

Sex: All·Age: Up to 1

Code: NCT04848090·Enrolling By Invitation

A Master Protocol (LY900023) That Includes Several Clinical Trials of Drugs for Children and Young Adults With Cancer

for Neoplasms

30 locations incl. Birmingham

Sponsor: Eli Lilly and Company

Sex: All·Age: 1 - 39

Code: NCT05999994·Phase 2·Recruiting

Apply to this trial

A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice

for Duchenne Muscular Dystrophy

20 locations incl. Little Rock

Sponsor: Sarepta Therapeutics, Inc.

Sex: Male·Age: All ages

Code: NCT06606340·Enrolling By Invitation

Mapping Disease Pathways for Biliary Atresia

for Biliary Atresia

1 location in Pittsburgh

Sponsor: University of Pittsburgh

Sex: All·Age: All ages

Code: NCT03273049·Recruiting

Apply to this trial

COMPASSION S3 - Evaluation of the SAPIEN 3 Transcatheter Heart Valve in Patients With Pulmonary Valve Dysfunction

for Complex Congenital Heart Defect

25 locations incl. Little Rock

Sponsor: Edwards Lifesciences

Sex: All·Age: All ages

Code: NCT02744677·Recruiting

Apply to this trial

Molecular Basis of Pediatric Liver Cancer

for Childhood Liver Cancer

1 location in Pittsburgh

Sponsor: University of Pittsburgh

Sex: All·Age: 0 - 99

Code: NCT03959800·Recruiting

Apply to this trial

Reduced Intensity Conditioning for Non-Malignant Disorders Undergoing UCBT, BMT or PBSCT

for Primary Immunodeficiency (PID)

1 location in Pittsburgh

Sponsor: Paul Szabolcs

Sex: All·Age: 2 Months - 55

Code: NCT01962415·Phase 2·Recruiting

Apply to this trial

Longitudinal Study of Neurodegenerative Disorders

for MLD

1 location in Pittsburgh

Sponsor: University of Pittsburgh

Sex: All·Age: All ages

Code: NCT03333200·Recruiting

Apply to this trial

Biliary Atresia Study in Infants and Children

for Biliary Atresia

15 locations incl. Los Angeles

Sponsor: Arbor Research Collaborative for Health

Sex: All·Age: 6 Months - 20

Code: NCT00345553·Recruiting

Apply to this trial

Clinical and Laboratory Study of Methylmalonic Acidemia

for Organic Acidemia

3 locations incl. Washington D.C.

Sponsor: National Human Genome Research Institute (NHGRI)

Sex: All·Age: 1 Month - 115·Accepts healthy volunteers

Code: NCT00078078·Recruiting

Apply to this trial

A Prospective Database of Infants With Cholestasis

for Biliary Atresia

15 locations incl. Los Angeles

Sponsor: Arbor Research Collaborative for Health

Sex: All·Age: Up to 6 Months

Code: NCT00061828·Recruiting

Apply to this trial