Natural History of Duchenne Muscular Dystrophy
- Sponsor
- Genethon
- Study ID
- NCT03882827
- Status
- Recruiting
Conditions
Eligibility Criteria
- Sex
- MALE
- Age
- 4 Years - 9 Years
- Healthy Volunteers
- Not accepted
Study Details
Baseline Study on Duchenne Muscular Dystrophy (DMD) in view to collect data on the natural disease course in a cohort in young male subjects aged from 4 to 9 Years over a period of 6 to 36 months using disease appropriate evaluations.
Key Dates
- First listed
- Mar 20, 2019
- Start date
- Dec 19, 2019
- Status verified
- Feb 2026
- Primary completion
- May 30, 2029
- Completion
- Sep 30, 2029
Study Design
- Enrollment
- 220 participants (estimated)
Primary Outcome Measure
NSAA scale [ Time Frame: Screening 36 months ]
Central Contacts
- Francesco MUNTONI, Pr+44 02079052602
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