Natural History of Duchenne Muscular Dystrophy

Sponsor
Genethon
Study ID
NCT03882827
Status
Recruiting

Conditions

Eligibility Criteria

Sex
MALE
Age
4 Years - 9 Years
Healthy Volunteers
Not accepted

Study Details

Baseline Study on Duchenne Muscular Dystrophy (DMD) in view to collect data on the natural disease course in a cohort in young male subjects aged from 4 to 9 Years over a period of 6 to 36 months using disease appropriate evaluations.

Key Dates

First listed
Mar 20, 2019
Start date
Dec 19, 2019
Status verified
Feb 2026
Primary completion
May 30, 2029
Completion
Sep 30, 2029

Study Design

Enrollment
220 participants (estimated)

Primary Outcome Measure

NSAA scale [ Time Frame: Screening 36 months ]

Central Contacts

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