Duchenne muscular dystrophy Clinical Trials

Recruiting duchenne muscular dystrophy studies with sites across the US, sourced from ClinicalTrials.gov and refreshed daily. Free to join — find one near you below.

Clinical trials study new ways to prevent, detect, or treat duchenne muscular dystrophy. Joining one can give you access to investigational treatments and close monitoring by a specialist research team — at no cost — while helping advance care for others. Below are recruiting duchenne muscular dystrophy studies with sites across the US; use the location tools to find ones near you.

What to expect

Screening first. The study team reviews your eligibility before anything else — there's no obligation to continue.
Informed consent. You'll get a full explanation of the study, its potential risks and benefits, and can withdraw at any time.
No cost to you. Study visits, tests, and the investigational treatment are covered; many studies reimburse travel.

Recruiting duchenne muscular dystrophy trials

Within

Safety and Efficacy of KER-065 in Participants With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Keros Therapeutics, Inc.

Sex: Male·Age: 9+

Code: NCT07704099·Phase 2

Study to Evaluate the Safety and Effectiveness of ELEVIDYS in Participants With Duchenne Muscular Dystrophy Treated in a Post-Marketing Setting

for Duchenne Muscular Dystrophy

Sponsor: Sarepta Therapeutics, Inc.

Sex: Male·Age: 4+

Code: NCT07542314·Phase 4

Open-Label Extension Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Wave Life Sciences USA, Inc.

Sex: Male·Age: All ages

Code: NCT07209332·Phase 2

Phase 2 Study of SAT-3247 in Pediatric Ambulatory Patients

for Duchenne Muscular Dystrophy

7 sites incl. Los Angeles

Sponsor: Satellos Bioscience, Inc.

Sex: Male·Age: 7 - 9

Code: NCT07287189·Phase 2

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A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

for Duchenne Muscular Dystrophy

3 sites incl. Little Rock

Sponsor: Solid Biosciences Inc.

Sex: Male·Age: 7 - 11

Code: NCT07160634·Phase 3

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A Study to Evaluate the Tolerability, Safety and Efficacy of GNR-097 Gene Therapy in Pediatric Patients With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: AO GENERIUM

Sex: Male·Age: 4 - 9

Code: NCT07673809·Phase 1, Phase 2

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A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

for Duchenne Muscular Dystrophy

10 sites incl. Little Rock

Sponsor: Insmed Gene Therapy LLC

Sex: Male·Age: 2 - 4

Code: NCT06817382·Phase 1

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Gamified Occupational Therapy for Adolescents With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Başak Çağla Arslan

Sex: Male·Age: 13 - 18

Code: NCT06402942

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Trial of Cell Based Therapy for DMD

for Duchenne Muscular Dystrophy

1 site in Minneapolis

Sponsor: Masonic Cancer Center, University of Minnesota

Sex: All·Age: 18+

Code: NCT06692426·Phase 1

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Investigation of the Relationship Between Executive Functions and Occupational Performance of Children With Duchenne Muscular Dystrophy

for Executive Dysfunction

Sponsor: Lokman Hekim University

Sex: Male·Age: 6 - 12·Accepts healthy volunteers

Code: NCT06868784

Effectiveness of 5-week Digital Respiratory Practice in Children With Duchenne and Becker Muscular Dystrophies.

for Duchenne Muscular Dystrophy

Sponsor: University of Malaga

Sex: All·Age: 5 - 20

Code: NCT06363526

Pharmacokinetics and Safety of Givinostat in DMD Patients Ages From at Least 2 Years to Less Then 6 Years Old

for Duchenne Muscular Dystrophy

Sponsor: Italfarmaco

Sex: Male·Age: 2 - 6

Code: NCT06769633·Phase 2

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Evaluation of Brain Dysfunction in Patients with Duchene Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Assiut University

Sex: Male·Age: 5 - 18·Accepts healthy volunteers

Code: NCT06732011

The U.K. NorthStar Clinical Network

for Duchenne Muscular Dystrophy

Sponsor: University College, London

Sex: Male·Age: Up to 99

Code: NCT06711692

Development of a Registry to Assess Natural History in Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Sex: Male·Age: All ages

Code: NCT06579859

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy-SUMMIT

for Duchenne Muscular Dystrophy

31 sites incl. Phoenix

Sponsor: Catalyst Pharmaceuticals, Inc.

Sex: Male·Age: 2+

Code: NCT06564974

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Applying the Pathways and Resources for Engagement and Participation Protocol Among People With Muscles Dystrophies

for Duchenne Muscular Dystrophy

Sponsor: University of Haifa

Sex: Male·Age: 14 - 30

Code: NCT06540365

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD - Longitudinal Aim

for Duchenne Muscular Dystrophy

1 site in Nashville

Sponsor: Vanderbilt University Medical Center

Sex: Male·Age: 10+

Code: NCT06093100

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FLOWER: Following Longitudinal Outcomes With Epidemiology for Rare Diseases

for Alpha-Thalassemia

1 site in Los Altos

Sponsor: xCures

Sex: All·Age: All ages

Code: NCT06539169

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Vasodilator and Exercise Study for DMD (VASO-REx)

for Duchenne Muscular Dystrophy

1 site in Gainesville

Sponsor: University of Florida

Sex: Male·Age: 6+

Code: NCT06290713·Phase 2

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Long Term Follow-up for RGX-202

for Duchenne Muscular Dystrophy

5 sites incl. Little Rock

Sponsor: REGENXBIO Inc.

Sex: Male·Age: All ages

Code: NCT06491927

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

for Duchenne Muscular Dystrophy

12 sites incl. Little Rock

Sponsor: Solid Biosciences Inc.

Sex: Male·Age: 0 - 17

Code: NCT06138639·Phase 1, Phase 2

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Respiratory Functions, Thoracoabdominal Movements and Exercise Capacity in Neuromuscular Diseases

for Neuromuscular Diseases in Children

Sponsor: Lokman Hekim University

Sex: All·Age: 5 - 15·Accepts healthy volunteers

Code: NCT06756633

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Wearable Technology to Evaluate Hyperglycemia and HRV in DMD

for Duchenne Muscular Dystrophy

1 site in Nashville

Sponsor: Vanderbilt University Medical Center

Sex: Male·Age: 10+·Accepts healthy volunteers

Code: NCT06124196

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NS-089/NCNP-02-201 in Boys With Duchenne Muscular Dystrophy (DMD)

for Duchenne Muscular Dystrophy

10 sites incl. Aurora

Sponsor: NS Pharma, Inc.

Sex: Male·Age: 4 - 14

Code: NCT05996003·Phase 2

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Efficacy, Safety and Tolerability of Givinostat in Non-ambulant Patients With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Italfarmaco

Sex: Male·Age: 9 - 17

Code: NCT05933057·Phase 3

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An Observational Study Comparing Delandistrogene Moxeparvovec (ELEVIDYS) With Standard of Care in Participants With Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

25 sites incl. Little Rock

Sponsor: Sarepta Therapeutics, Inc.

Sex: Male·Age: 4+

Code: NCT06270719

A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Clinical Study

for Duchenne Muscular Dystrophy

22 sites incl. Little Rock

Sponsor: Sarepta Therapeutics, Inc.

Sex: Male·Age: All ages

Code: NCT05967351·Phase 3

Psychoeducation Program for Parents of Children with Duchenne Muscular Dystrophy

for Psychoeducation

Sponsor: Lokman Hekim University

Sex: All·Age: 18 - 65

Code: NCT06412328

Follow-up Study on Female Carriers With DMD Gene Variants

for Muscular Dystrophy

Sponsor: Rigshospitalet, Denmark

Sex: All·Age: 18+

Code: NCT05715957

phenotypeS in Non Ambulant Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Fondazione Policlinico Universitario Agostino Gemelli IRCCS

Sex: Male·Age: 8 - 35

Code: NCT06366815

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Open-label Study of WVE-N531 in Patients With Duchenne Muscular Dystrophy (FORWARD-53)

for Duchenne Muscular Dystrophy

2 sites incl. Little Rock

Sponsor: Wave Life Sciences USA, Inc.

Sex: Male·Age: 4 - 18

Code: NCT04906460·Phase 1, Phase 2

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CureDuchenne Link®: A Resource for Research

for Duchenne Muscular Dystrophy

10 sites incl. Little Rock

Sponsor: CureDuchenne

Sex: All·Age: 4 Weeks+

Code: NCT04972604

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Once Weekly Infant Corticosteroid Trial for DMD

for Duchenne Muscular Dystrophy

4 sites incl. Chicago

Sponsor: Anne M. Connolly

Sex: Male·Age: 1 Month - 30 Months

Code: NCT05412394·Phase 4

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A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

for Duchenne Muscular Dystrophy

6 sites incl. Little Rock

Sponsor: Sarepta Therapeutics, Inc.

Sex: Male·Age: 2+

Code: NCT04626674·Phase 1

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Magnetic Resonance Imaging and Biomarkers for Muscular Dystrophy

for Duchenne Muscular Dystrophy

2 sites incl. Gainesville

Sponsor: University of Florida

Sex: Male·Age: 5 - 62·Accepts healthy volunteers

Code: NCT01484678

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Assessments in Patients With Muscular Pathology and in Control Subjects : The ActiLiège Next Study

for Duchenne Muscular Dystrophy

Sponsor: Centre Hospitalier Universitaire de Liege

Sex: All·Age: 1 - 80·Accepts healthy volunteers

Code: NCT05982119

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Natural History of Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Genethon

Sex: Male·Age: 4 - 9

Code: NCT03882827

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Extracellular RNA Biomarkers of Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

1 site in Boston

Sponsor: Massachusetts General Hospital

Sex: All·Age: 5+

Code: NCT05016908

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A Registered Cohort Study on Duchenne Muscular Dystrophy

for Duchenne Muscular Dystrophy

Sponsor: Ning Wang, MD., PhD.

Sex: All·Age: 2+

Code: NCT04012671

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A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice

for Duchenne Muscular Dystrophy

20 sites incl. Little Rock

Sponsor: Sarepta Therapeutics, Inc.

Sex: Male·Age: All ages

Code: NCT06606340

Parent and Infant Inter(X)Action Intervention (PIXI)

for Fragile X Syndrome

1 site in Research Triangle Park

Sponsor: RTI International

Sex: All·Age: Up to 99·Accepts healthy volunteers

Code: NCT03836300

Givinostat in Duchenne's Muscular Dystrophy Long-term Safety and Tolerability Study

for Duchenne Muscular Dystrophy

2 sites incl. Atlanta

Sponsor: Italfarmaco

Sex: Male·Age: 7+

Code: NCT03373968·Phase 2, Phase 3

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Biomarker Development for Muscular Dystrophies

for Myotonic Dystrophy

4 sites incl. Boston

Sponsor: Massachusetts General Hospital

Sex: All·Age: 5+·Accepts healthy volunteers

Code: NCT05019625

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The Duchenne Registry

for Duchenne Muscular Dystrophy

1 site in Washington D.C.

Sponsor: The Duchenne Registry

Sex: All·Age: All ages

Code: NCT02069756

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Duchenne muscular dystrophy clinical trials — common questions

Are duchenne muscular dystrophy clinical trials free to join?

Yes. Participating in a duchenne muscular dystrophy clinical trial is free — study-related visits, tests, and the investigational treatment are provided at no cost to you. Many studies also reimburse travel and time. You never pay to take part.

Who can join a duchenne muscular dystrophy clinical trial?

Each duchenne muscular dystrophy study sets its own eligibility criteria — typically based on age, medical history, current treatments, and overall health. Every trial listed here shows its criteria, and the study team confirms your eligibility before enrollment. You can review and apply to any that look like a fit.

How do I find a duchenne muscular dystrophy trial near me?

Use the location controls above. We'll show recruiting duchenne muscular dystrophy trials with sites near you, sorted by distance. You can widen the radius or share your exact location for the closest matches.

How many duchenne muscular dystrophy trials are recruiting right now?

We're currently tracking roughly 28 recruiting duchenne muscular dystrophy trials with US sites, sourced from ClinicalTrials.gov and refreshed daily.

Looking for a specific location? Browse trials by city and state.

Duchenne muscular dystrophy trials by city

Little Rock, AR Boston, MA Gainesville, FL Aurora, CO Chicago, IL Los Angeles, CA

Related specialties

Pediatrics