A Registered Cohort Study on Duchenne Muscular Dystrophy

Sponsor
Ning Wang, MD., PhD.
Study ID
NCT04012671
Status
Recruiting
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Conditions

Eligibility Criteria

Sex
ALL
Age
2 Years - N/A
Healthy Volunteers
Not accepted

Study Details

Dystrophinopathy is a term of X-linked recessive genetic disease, including Duchenne Muscular Dystrophy, Becker Muscular Dystrophy, and the X-linked dilated cardiomyopathy. The aim of this study is to determine the clinical spectrum and natural progression of dystrophinopathy in a prospective multicenter natural history study, to assess the clinical, genetic of patients with dystrophinopathy to optimize clinical management.

Key Dates

First listed
Jul 9, 2019
Start date
Jul 1, 2019
Status verified
Feb 2021
Primary completion
Dec 31, 2039
Completion
Dec 31, 2049

Study Design

Enrollment
2,000 participants (estimated)

Primary Outcome Measure

Age at death [ Time Frame: 20 years ]

Central Contacts

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