RESET-MG: A Study to Evaluate the Safety and Efficacy of CABA-201 in Participants With Generalized Myasthenia Gravis

Part of paid clinical trials in Orange, California.

Sponsor
Cabaletta Bio
Study ID
NCT06359041
Phase
PHASE1/PHASE2
Status
Recruiting

Conditions

  • Generalized Myasthenia Gravis (gMG)

Eligibility Criteria

Sex
ALL
Age
18 Years - 70 Years
Healthy Volunteers
Not accepted

Interventions

  • CABA-201 — BIOLOGICAL
    Single intravenous infusion of CABA-201 at a single dose level following preconditioning with fludarabine and cyclophosphamide
  • CABA-201 — BIOLOGICAL
    Single intravenous infusion of CABA-201 at escalating dose levels without preconditioning

Study Details

RESET-MG: A Phase 1/2 Open-Label Study to Evaluate the Safety and Efficacy of CABA-201 in Participants with Generalized Myasthenia Gravis

Key Dates

First listed
Apr 11, 2024
Start date
Dec 17, 2024
Status verified
Aug 2026
Primary completion
Sep 30, 2029
Completion
Sep 30, 2029

Study Design

Enrollment
24 participants (estimated)
Allocation
NON_RANDOMIZED
Intervention model
SINGLE_GROUP
Primary purpose
TREATMENT

Arms

  • Experimental: CABA-201
    AChR Antibody-Positive Cohort or AChR Antibody-Negative Cohort
  • Experimental: CABA-201, No Preconditioning
    Infusion of CABA-201 with no preconditioning in subjects with gMG

Primary Outcome Measure

To evaluate incidence and severity of adverse events (AEs) [ Time Frame: Up to 28 days after CABA-201 infusion ]

Central Contacts

Locations (17)

FacilityCityStateZIPSite coordinators
University of California IrvineOrangeCalifornia92868
Alpha Clinic
949-824-3990
Ali Habib, MD (PRINCIPAL_INVESTIGATOR)
UC Davis, Department of NeurologySacramentoCalifornia95817
Sahar Jammal
916-734-1798
David Richman, MD (PRINCIPAL_INVESTIGATOR)
University of California, San FranciscoSan FranciscoCalifornia94143
Zane Ashkar
415-501-0671
Dr. Min Kang, MD (PRINCIPAL_INVESTIGATOR)
University of ColoradoAuroraColorado80045
Recruitment Specialist
303-724-4644
Alyssa Alviez
Amanda Piquet, MD (PRINCIPAL_INVESTIGATOR)
Mayo Clinic FloridaJacksonvilleFlorida32224
Huy Tran CRC
904-953-4503
Dr. Jaimin Shah, MD (PRINCIPAL_INVESTIGATOR)
Northwestern Memorial HospitalChicagoIllinois60611
Kaitlin King
312-921-2371
Dr. Arjun Seth, MD (PRINCIPAL_INVESTIGATOR)
University of Kansas Medical CenterKansas CityKansas66160
Lilli Saavedra
913-945-9937
Mazen Dimachkie, MD (PRINCIPAL_INVESTIGATOR)
Beth Israel Deaconess Medical CenterBostonMassachusetts02215
Amy Lewandowski
617-667-2545
Pushpa Narayanaswami, MD (PRINCIPAL_INVESTIGATOR)
University of Massachusetts Chan Medical SchoolWorcesterMassachusetts01655
Catherine Douthwright
508-856-1524
Dr. Margaret A. Owegi, DO (PRINCIPAL_INVESTIGATOR)
Mayo Clinic - RochesterRochesterMinnesota55905
Bridget Neja
507-266-9150
Elie Naddaf, M.D. (PRINCIPAL_INVESTIGATOR)
Columbia UniversityNew YorkNew York10032
CPDM Nursing Navigator
212-342-5162
Dr. Christina Ulane, MD (PRINCIPAL_INVESTIGATOR)
University of Rochester Medical CenterRochesterNew York14642
Olivia Tauriello
585-275-3707
Dr. Alexis Lizarraga, MD, MS (PRINCIPAL_INVESTIGATOR)
Oregon Health & Science UniversityPortlandOregon97239
Katie Lewis
503-494-7394
Dr. Nizar Chahin, M.D. (PRINCIPAL_INVESTIGATOR)
Baylor College of Medicine Neurology DepartmentHoustonTexas77030
Victoria Herrick
713-798-5670
Milvia Pleitez, MD (PRINCIPAL_INVESTIGATOR)
Houston Methodist HospitalHoustonTexas77030
Delrose A Vernon, BS, MBA, CCRP
346-238-8226
Dr. Sheetal Shroff, MD (PRINCIPAL_INVESTIGATOR)
University of Texas MD Anderson Cancer CenterHoustonTexas77030
Meredith del Rosario
713-792-1416
Uday Popat, MD (PRINCIPAL_INVESTIGATOR)
Swedish Neuroscience ResearchSeattleWashington98122
Desiree Iriarte
206-320-2282
Dr. Christyn Edmundson, MD (PRINCIPAL_INVESTIGATOR)

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