phenotypeS in Non Ambulant Duchenne Muscular Dystrophy

Sponsor
Fondazione Policlinico Universitario Agostino Gemelli IRCCS
Study ID
NCT06366815
Status
Recruiting
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Conditions

Eligibility Criteria

Sex
MALE
Age
8 Years - 35 Years
Healthy Volunteers
Not accepted

Interventions

  • Different Phenotypes of non ambulant patients with Duchenne Muscular Dystrophy — OTHER
    clinical and functional data collection of non ambulant patients with Duchenne muscular dystrophy

Study Details

The aims of the study are to prospectively collect information on several aspects of function in non-ambulant DMD patients by using a structured battery of tests including motor, respiratory and cardiac function

Key Dates

First listed
Apr 16, 2024
Start date
Aug 30, 2022
Status verified
Oct 2024
Primary completion
Sep 30, 2024
Completion
Dec 30, 2025

Study Design

Enrollment
250 participants (estimated)

Primary Outcome Measure

motor function [ Time Frame: 24 months ]

Central Contacts

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