Study of SAR447537 (INBRX-101) Compared to Plasma-derived A1PI Therapy in Adults With AATD Emphysema

Part of paid clinical trials in Birmingham, Alabama.

Sponsor
Sanofi
Study ID
NCT05856331
Phase
PHASE2
Status
Completed

Conditions

Eligibility Criteria

Sex
ALL
Age
18 Years - 80 Years
Healthy Volunteers
Not accepted

Interventions

  • SAR447537 — DRUG
    A1PI, Recombinant, Bivalent Fc Fusion Protein
  • Zemaira — DRUG
    Alpha1-Proteinase Inhibitor (Human)

Study Details

Phase 2 study to compare SAR447537 (INBRX-101) to plasma derived A1PI therapy in adults with AATD emphysema

Key Dates

First listed
May 12, 2023
Start date
Oct 12, 2023
Status verified
Aug 2025
Primary completion
Aug 6, 2025
Completion
Aug 6, 2025

Study Design

Enrollment
99 participants (actual)
Allocation
RANDOMIZED
Intervention model
PARALLEL
Primary purpose
TREATMENT

Arms

  • Experimental: SAR447537 (INBRX-101) Q3W
    IV every 3-weeks (Q3W) and placebo (normal saline)
  • Experimental: SAR447537 (INBRX-101) Q4W
    IV every 4-weeks (Q4W) and placebo (normal saline)
  • Active Comparator: Zemaira (A1PI)
    60 mg/kg IV once weekly (QW) and placebo (normal saline)

Primary Outcome Measure

Serum functional AAT (fAAT) levels at steady-state [ Time Frame: 32 Weeks ]

Locations (39)

FacilityCityStateZIPSite coordinators
University of Alabama at BirminghamBirminghamAlabama35249-
University of Alabama at Birmingham- Site Number : 105BirminghamAlabama35233-2110-
St Joseph's Hospital and Medical CenterPhoenixArizona85013-4220-
St Joseph's Hospital and Medical Center- Site Number : 126PhoenixArizona85013-4220-
David Geffen School of MedicineLos AngelesCalifornia90095-
David Geffen School of Medicine- Site Number : 124Los AngelesCalifornia90095-3075-
UC Davis Comprehensive Cancer Center- Site Number : 110SacramentoCalifornia95817-
UC Davis Medical CenterSacramentoCalifornia95817-
National Jewish Medical and Research CenterDenverColorado80206-
National Jewish Medical and Research Center- Site Number : 123DenverColorado80206-2761-
Western Connecticut Medical GroupDanburyConnecticut06810-
University of FloridaGainesvilleFlorida32610-
University of Florida College of Medicine- Site Number : 101GainesvilleFlorida32610-
Bruce W. Carter Miami VA Medical Center - NAVREF - PPDS- Site Number : 114MiamiFlorida33125-1624-
University of MiamiMiamiFlorida33136-
Pulmonary and Sleep of Tampa BayTampaFlorida33607-
Pulmonary and Sleep of Tampa Bay- Site Number : 115TampaFlorida33607-6316-
Loyola University Medical CenterMaywoodIllinois60153-
Loyola University Medical Center- Site Number : 112MaywoodIllinois60153-
Indiana UniversityIndianapolisIndiana46202-5128-
M Health Fairview Clinics and Surgery Center - MinneapolisMinneapolisMinnesota55455-4800-
M Health Fairview Clinics and Surgery Center - Minneapolis- Site Number : 125MinneapolisMinnesota55455-4800-
Hannibal ClinicHannibalMissouri63401-
Hannibal Regional Healthcare System-HRMG-Hannibal- Site Number : 111HannibalMissouri63401-6890-
Columbia University Irving Medical Center- Site Number : 104New YorkNew York10032-
Oregon Health and Science UniversityPortlandOregon97239-
Oregon Health and Science University- Site Number : 117PortlandOregon97239-
Clinical Research Associates Of Central PA , LLCDuBoisPennsylvania15801-2277-
Clinical Research Associates Of Central PA , LLC- Site Number : 128DuBoisPennsylvania15801-2277-
Penn State Health Milton S. Hershey Medical CenterHersheyPennsylvania17033-
Penn State Health Milton S. Hershey Medical Center- Site Number : 122HersheyPennsylvania17033-2360-
Temple University HospitalPhiladelphiaPennsylvania19140-
Temple University Hospital- Site Number : 130PhiladelphiaPennsylvania19140-
Velocity Clinical Research - Spartanburg - PPDSSpartanburgSouth Carolina29303-
Velocity Clinical Research - Spartanburg - PPDS- Site Number : 120SpartanburgSouth Carolina29303-4225-
Houston Methodist HospitalHoustonTexas77030-
Houston Methodist Hospital- Site Number : 113HoustonTexas77030-
University of Utah HealthSalt Lake CityUtah84108-
University of Utah Health Care- Site Number : 106Salt Lake CityUtah84132-0001-

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